⇒ Treatment of transfusion-dependent beta-thalassemia (TDT) in patients 12 yrs and older👏
⇒ One-time treatment⭐
ℹ️ Drug info:
• CASGEVY™ (exagamglogene autotemcel [exa-cel])
⇒ PDUFA goal date: 3/30/24
⇒ BLA
⇒ Transfusion-dependent beta-thalassemia (TDT)
⇒ CRISPR/Cas9 gene-edited cell therapy